Abstract
The ability of hematopoietic stem cells (HSCs) to engraft in a recipient and establish long-term repopulation of the hematopoietic system makes them ideal targets for gene therapy vectors designed to correct inherited or acquired diseases affecting the hematopoietic and immune systems.
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Swaney, W.P., Novelli, E.M., Bahnson, A.B., Barranger, J.A. (2002). Retrovirus-Mediated Gene Transfer to Human Hematopoietic Stem Cells. In: Morgan, J.R. (eds) Gene Therapy Protocols. Methods in Molecular Medicine, vol 69. Springer, Totowa, NJ. https://doi.org/10.1385/1-59259-141-8:187
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DOI: https://doi.org/10.1385/1-59259-141-8:187
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