Potential of Artificial Intelligence to Accelerate Drug Development for Rare Diseases
Authors (first, second and last of 5)
Collection
Rare Diseases
Topical issues in rare diseases.
Articles (6 in this collection)
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Eliciting Exploratory Patient Preference Data: A Case Study in a Rare Disease
Authors (first, second and last of 5)
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Embedding Patient-Centricity by Collaborating with Patients to Transform the Rare Disease Ecosystem
Authors (first, second and last of 5)
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Somatic Gene Therapy Research in Pediatric Populations: Ethical Issues and Guidance for Operationalizing Early Phase Trials
Authors (first, second and last of 5)
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Medical Research Charities and Biopharmaceutical Companies as Partners in Patient-Centred R&D
Authors (first, second and last of 6)
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Establishing Patient Registries for Rare Diseases: Rationale and Challenges
Authors (first, second and last of 5)
