Approaches to the Treatment of the Hemoglobin Disorders
Many of the hemoglobin disorders, particularly those that include the sickle hemoglobinopathies and thalassemia syndromes, produce severe disease manifestations and early mortality in a large percentage of affected individuals. The disability, pain, and loss of productivity that these individuals suffer, as well as their often extensive needs for transfusions and other forms of medical care, have stimulated major efforts toward the development of more effective forms of therapy for these conditions.
KeywordsSickle Cell Disease Sickle Cell Globin Gene Cytosine Arabinoside Thalassemia Patient
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