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Bone Marrow Transplantation in the Treatment of Lysosomal Storage Diseases

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Summary

Since 1980, bone marrow transplantation has been used in the treatment of children and young adults suffering from lysosomal enzyme deficiencies. Different animal models of lysosomal storage diseases have been investigated. This chapter describes the possible contribution of bone marrow transplantation in the treatment of subjects with such diseases. So far, these procedures must be considered as experimental, having mainly a beneficial effect on non-neurologic visceral tissues.

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Authors
  1. P. M. Hoogerbrugge
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  2. J. M. J. J. Vossen
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Editor information

Editors and Affiliations

  1. Department of Pediatrics, University Hospital, Oostersingel 59, 9713 EZ, Groningen, The Netherlands

    John Fernandes M. D. (Professor of Pediatrics) (Professor of Pediatrics)

  2. Clinique de Génétique Médicale, Hôpital des Enfants Malades, 149, rue de Sèvres, 75743, Paris Cedex, France

    Jean-Marie Saudubray M. D. (Professor of Pediatrics) (Professor of Pediatrics)

  3. Department of Pediatrics, Tohoku University, School of Medicine, 1-1 Seiryo-machi, Sendai 980, Japan

    Keiya Tada M. D. (Professor of Pediatrics) (Professor of Pediatrics)

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© 1990 Springer-Verlag Berlin Heidelberg

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Hoogerbrugge, P.M., Vossen, J.M.J.J. (1990). Bone Marrow Transplantation in the Treatment of Lysosomal Storage Diseases. In: Fernandes, J., Saudubray, JM., Tada, K. (eds) Inborn Metabolic Diseases. Springer, Berlin, Heidelberg. https://doi.org/10.1007/978-3-662-02613-7_52

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  • DOI: https://doi.org/10.1007/978-3-662-02613-7_52

  • Publisher Name: Springer, Berlin, Heidelberg

  • Print ISBN: 978-3-662-02615-1

  • Online ISBN: 978-3-662-02613-7

  • eBook Packages: Springer Book Archive

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