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Bone Marrow Transplantation in the Treatment of Lysosomal Storage Diseases

  • P. M. Hoogerbrugge
  • J. M. J. J. Vossen

Summary

Since 1980, bone marrow transplantation has been used in the treatment of children and young adults suffering from lysosomal enzyme deficiencies. Different animal models of lysosomal storage diseases have been investigated. This chapter describes the possible contribution of bone marrow transplantation in the treatment of subjects with such diseases. So far, these procedures must be considered as experimental, having mainly a beneficial effect on non-neurologic visceral tissues.

Keywords

Bone Marrow Transplantation Allogeneic Bone Marrow Transplantation Lysosomal Storage Disease Metachromatic Leukodystrophy Gauche Cell 
These keywords were added by machine and not by the authors. This process is experimental and the keywords may be updated as the learning algorithm improves.

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Copyright information

© Springer-Verlag Berlin Heidelberg 1990

Authors and Affiliations

  • P. M. Hoogerbrugge
  • J. M. J. J. Vossen

There are no affiliations available

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