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Mögliche Techniken für eine Hämophilie-Gentherapie

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24. Hämophilie-Symposion

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Zusammenfassung

Die Hämophilie wird durch teilweise funktionsunfähige oder nicht vorhandene Gerinnungsproteine ausgelöst. Ist das Faktor VIII-Protein defekt, liegt eine Hämophilie A vor. Ist dagegen das Faktor IX-Protein defekt, spricht man von einer Hämophilie B. Beide Erbkrankheiten werden durch Mutationen im Faktor VIII- bzw. Faktor IX-Gen ausgelöst [1, 2].

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Authors
  1. R. Schwaab
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  2. J.-P. Faber
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  3. J. Oldenburg
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  4. H.-H. Brackmann
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Editor information

Editors and Affiliations

  1. Abteilung für Angiologie, Zentrum der Inneren Medizin, Klinikum der Johann-Wolfgang-Goethe-Universität, Theodor-Stern-Kai 7, D-60590, Frankfurt am Main, Germany

    Inge Scharrer

  2. Hämostaseologische Abteilung, Medizinische Klinik, Klinikum Innenstadt der Ludwig-Maximilians-Universität, Ziemssenstraße 1a, D-80336, München, Germany

    Wolfgang Schramm

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© 1994 Springer-Verlag Berlin Heidelberg

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Schwaab, R., Faber, JP., Oldenburg, J., Brackmann, HH. (1994). Mögliche Techniken für eine Hämophilie-Gentherapie. In: Scharrer, I., Schramm, W. (eds) 24. Hämophilie-Symposion. Springer, Berlin, Heidelberg. https://doi.org/10.1007/978-3-642-79009-6_20

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  • DOI: https://doi.org/10.1007/978-3-642-79009-6_20

  • Publisher Name: Springer, Berlin, Heidelberg

  • Print ISBN: 978-3-540-57999-1

  • Online ISBN: 978-3-642-79009-6

  • eBook Packages: Springer Book Archive

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