Opportunities for the Use of Lentiviral Vectors in Human Gene Therapy
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The quest for the perfect delivery system has been one of the leitmotivs in the young history of gene therapy. Remarkable progress in vector design has generated a number of distinct viral and nonviral gene delivery tools, each manifesting advantages and distinct limitations.
KeywordsGene Therapy Retinitis Pigmentosa Equine Infectious Anemia Virus Ciency Virus Metachromatic Leukodystrophy
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