American Cancer Society. Cancer facts & figures 2014. Atlanta: American Cancer Society; 2014.
Google Scholar
American Society of Clinical Oncology. The state of cancer care in America, 2014: a report by the American Society of Clinical Oncology. J Oncology Pract. 2014;10(2):119–42.
CrossRef
Google Scholar
Reichert JM, Wenger JB. Development trends for new cancer therapeutics and vaccines. Drug Discov Today. 2008;13:30–7.
CAS
CrossRef
PubMed
Google Scholar
Institute of Medicine. Ensuring quality cancer care. Washington, DC: National Academies Press; 1999.
Google Scholar
Bosanquet N, Sikora K. The economics of cancer care. New York: Cambridge University Press; 2006.
CrossRef
Google Scholar
Wilensky GR. Developing a center for comparative effectiveness information. Health Aff. 2006;25:w572–85.
CrossRef
Google Scholar
Institute of Medicine. Assessing and improving value in cancer care: workshop summary. Washington, DC: National Academies Press; 2009.
Google Scholar
Elkin EB, Bach PB. Cancer’s next frontier: addressing high and increasing costs. J Amer Med Assoc. 2010;303:1086–7.
CrossRef
Google Scholar
Kantarjian HM, Fojo T, Mathisen M, et al. Cancer drugs in the United States: Justum pretium – The just price. J Clin Oncol. 2013;31:3600–04.
CrossRef
PubMed
PubMed Central
Google Scholar
Skrepnek GH. Balancing cost, quality, and access to care among payers, providers, and patients: the Sword of Damocles. Az Med. 2008;19:18–27.
Google Scholar
Kissick WL. Medicine’s dilemmas: infinite needs versus finite resources. New Haven: Yale University Press; 1994.
Google Scholar
Donabedian A. Evaluating the quality of medical care. Milbank Mem Fund Q. 1966;44:166–206.
CrossRef
PubMed
Google Scholar
Donabedian A. Explorations in quality assessment and monitoring. Vol. I. The definition of quality and approaches to its assessment. Ann Arbor: Health Administration Press; 1980.
Google Scholar
Donabedian A. Explorations in quality assessment and monitoring. Vol. II. The criteria and standards of quality. Ann Arbor: Health Administration Press; 1982.
Google Scholar
Donabedian A. Explorations in quality assessment and monitoring. Vol. III. The methods and findings of quality assessment and monitoring: an illustrated analysis. Ann Arbor: Health Administration Press; 1985.
Google Scholar
Begley CE, Lairson DR, Morgan RO, Rowan PJ, Balkrishnan R. Evaluating the healthcare system: effectiveness, efficiency, and equity. 4th ed. Chicago: Health Administration Press; 2013.
Google Scholar
Institute of Medicine. Crossing the quality chasm: a new health system for the 21st century. Washington, DC: National Academy Press; 2001.
Google Scholar
Institute of Medicine. Priority areas for national action: transforming health care quality. Washington, DC: National Academy Press; 2003.
Google Scholar
World Health Organization. The World Health Report 2000 – health systems: improving performance. Geneve: World Health Organization; 2000.
Google Scholar
Clancy CM, Eisenberg JM. Outcomes research: measure the end results of health care. Science. 1998;282:245–6.
CAS
CrossRef
PubMed
Google Scholar
Lipscomb J, Donaldson MS, Hiatt RA. Cancer outcomes research and the arenas of application. Natl Cancer Inst Monogr. 2004;33:1–7.
CrossRef
Google Scholar
Agency for Healthcare Research and Quality. Outcomes research fact sheet: What is outcomes research? Internet: http://www.ahrq.gov/clinic/outfact.htm.
Lipscomb J, Snyder CF. The outcomes of cancer outcomes research. Med Care. 2002;40S:III3–10.
Google Scholar
Lipscomb J, Donaldson MS. Outcomes research at the National Cancer Institute: measuring, understanding, and improving the outcomes of cancer care. Clin Ther. 2003;25:699–712.
CrossRef
PubMed
Google Scholar
Kozma CM, Reeder CE, Schulz RM. Economic, clinical, and humanistic outcomes: a planning model for pharmacoeconomic research. Clin Ther. 1993;15:1121–32.
CAS
PubMed
Google Scholar
Skrepnek GH. Cost-effectiveness analysis. In: Bootman JL, Townsend RJ, McGhan WF, editors. Principles of pharmacoeconomics. 3rd ed. Cincinnati: W Harvey Whitney Books; 2005. p. 83–116.
Google Scholar
Evans DB, Tandon A, Murray CJL, Lauer JA. Comparative efficiency of National Health Systems in Producing Health: an analysis of 191 Countries, GPE discussion paper series no. 29. Geneve: World Health Organization; 2001.
Google Scholar
Fishman J, Skrepnek GH. Pharmacoeconomic analyses of treatments for rare disease. Pharm Policy Law. 2012;14:51–67.
Google Scholar
Tate WR, Skrepnek GH. Quality-Adjusted Time Without Symptoms or Toxicity (Q-TWiST): patient reported outcome or mathematical model? A systematic review in cancer. Psychooncology. 2014. doi:10.1002/pon.359.
PubMed
Google Scholar
Havrilesky LJ, Fountain C. Can we maximize both value and quality in gynecologic cancer care? A work in progress. ASCO educational book. Alexandria: American Society of Clinical Oncology; 2014. p. e268–75.
Google Scholar
Schumock GT, Pickard AS. Comparative effectiveness research. Amer J Health-Systems Pharm. 2009;66:e2–10.
Google Scholar
Institute of Medicine. Knowing what works in health care: a roadmap for the nation. Washington, DC: National Academies Press; 2008.
Google Scholar
Institute of Medicine. Initial national priorities for comparative effectiveness research. Washington, DC: National Academies Press; 2009.
Google Scholar
Tunis SR, et al. Practical clinical trials: increasing the value of clinical research for decision making in clinical and health policy. J Amer Med Assoc. 2003;290:1624–32.
CAS
CrossRef
Google Scholar
Vermeulen LC, Beis SJ, Cano SB. Applying outcomes research in improving the medication-use process. Am J Health-Syst Pharm. 2000;57:2277–82.
CAS
PubMed
Google Scholar
Bootman JL, Skrepnek GH. Achieving value: the role of pharmacoeconomics. Pharm Policy Law. 2012;14:3–6.
Google Scholar
Dougherty CJ. Review of economics and ethics in health care. The Hippocratic predicament: affordability, access and accountability in American medicine, by Kaplan RM. N Engl J Med. 1993;328:1358–59.
CrossRef
Google Scholar
Brown ML, Lipscomb J, Snyder C. The burden of illness of cancer: economic cost and quality of life. Annu Rev Public Health. 2001;22:91–113.
CAS
CrossRef
PubMed
Google Scholar
Hodgson TA. The state of the art cost-of-illness studies. Adv Health Econ Health Serv Res. 1983;4:129–64.
CAS
PubMed
Google Scholar
Hodgson TA. Cost-of-illness in cost-effectiveness analysis: a review of the methodology. Pharmacoeconomics. 1994;6:536–52.
CAS
CrossRef
PubMed
Google Scholar
Rice DP. Cost-of-illness studies: fact or fiction? Lancet. 1994;344:1519–20.
CAS
CrossRef
PubMed
Google Scholar
Lipscomb J, Gotay CC, Snyder C, editors. Outcomes assessment in cancer: measures, methods, and applications. New York: Cambridge University Press; 2004.
Google Scholar
Trueman P, Drummond M, Hutton J. Developing guidance for budget impact analysis. Pharmacoeconomics. 2001;19:609–21.
CAS
CrossRef
PubMed
Google Scholar
Orlewska E, Gula’csi L. Budget-impact analyses a critical review of published studies. Pharmacoeconomics. 2009;27:807–27.
CrossRef
PubMed
Google Scholar
Drummond MF, Sculper MJ, Torrance GW, O’Brien BJ, Stoddard GL. Methods for the economic evaluation of health care programmes. 3rd ed. Cambridge: Oxford University Press; 2005.
Google Scholar
Bootman JL, Townsend RJ, McGhan WF, editors. Principles of pharmacoeconomics. 3rd ed. Cincinnati: W Harvey Whitney Books; 2005. p. 83–116.
Google Scholar
Briggs AH, O’Brien BJ. The death of cost-minimization analysis? Health Econ. 2001;10:179–84.
CAS
CrossRef
PubMed
Google Scholar
Fenwick E, Claxton K, Sculpher M. Representing uncertainty: the role of cost-effectiveness acceptability curves. Health Econ. 2001;10:779–87.
CAS
CrossRef
PubMed
Google Scholar
Kind P, Lafata JE, Matuszewski K, Raisch D. The use of QALYs in clinical and patient decision-making: issues and prospects. Value Health. 2009;12:S27–30.
CrossRef
PubMed
Google Scholar
Räsänen P, Roine E, Sintonen H, Semberg-Konttinen V, Ryynänen OP, Roine R. Use of quality-adjusted life years for the estimation of effectiveness of health care: a systematic literature review. Int J Technol Assess Health Care. 2006;22:235–41.
CrossRef
PubMed
Google Scholar
von Neumann J, Morgenstern O. Theory of games and economic behavior. Princeton: Princeton University Press; 1953.
Google Scholar
Horsman J, Furlong W, Feeny D, Torrance G. The Health Utilities Index (HUI®): concepts. Measurement properties and applications. Health Qual Life Outcomes. 2003;1:54.
CrossRef
PubMed
PubMed Central
Google Scholar
Kind P, Dolan P, Gudex C, et al. Variations in population health status: results from a United Kingdom National Questionnaire Survey. BMJ. 1998;316:736–41.
CAS
CrossRef
PubMed
PubMed Central
Google Scholar
Rabin R, de Charro F. EQ-5D: a measure of health status from the EuroQol group. Ann Med. 2001;33:337–43.
CAS
CrossRef
PubMed
Google Scholar
Turner-Bowker DM, Bartley PJ, Ware Jr JE. SF-36® health survey & “SF” bibliography: third edition (1988–2000). Lincoln: QualityMetric Incorporated; 2002.
Google Scholar
Bleichrodt H, Johannesson M. Standard gamble, time trade-off and rating scale: experimental results on the ranking properties of QALYs. J Health Econ. 1997;16:155–75.
CAS
CrossRef
PubMed
Google Scholar
Coons SJ, Rao S, Keininger DL, et al. A comparative review of generic quality-of-life instruments. Pharmacoeconomics. 2000;17:13–35.
CAS
CrossRef
PubMed
Google Scholar
Wilke RJ, Burke LB, Erickson P. Measuring treatment impact: a review of patient-reported outcomes and other efficacy endpoints in approved product labels. Control Clin Trials. 2004;25:535–52.
CrossRef
Google Scholar
Kaplan RM, Bush JW, Berry CC. Health status: types of validity and the index of well-being. Health Serv Res. 1976;11:478–507.
CAS
PubMed
PubMed Central
Google Scholar
Kaplan RM, Sieber WJ, Ganiats TG. The quality of well-being scale: comparison of the interviewer-administered version with a self-administered questionnaire. Psych Health. 1997;12:783–91.
CrossRef
Google Scholar
Hunt SM, McKenna SP, McEwen J, Backett EM, Williams J, Papp E. A quantitative approach to perceived health status: a validation study. J Epidemiol Community Health. 1980;34:281–6.
CAS
CrossRef
PubMed
PubMed Central
Google Scholar
Jenkinson C, Fitzpatrick R, Argyle M. The Nottingham Health Profile: an analysis of its sensitivity in differentiating illness groups. Soc Sci Med. 1988;27:1411–4.
CAS
CrossRef
PubMed
Google Scholar
Hunt SM, McKenna SP, McEwen J, Williams J, Papp E. The Nottingham Health Profile: subjective health status and medical consultations. Soc Sci Med. 1981;15:221–9.
CAS
Google Scholar
Bergner M, Bobbitt RA, Carter WB, Gilson BS. The sickness impact profile: development and final revision of a health status measure. Med Care. 1981;19:787–805.
CAS
CrossRef
PubMed
Google Scholar
Gilson BS, Gilson JS, Bergner M, Bobbit RA, Kressel S, Pollard WE, et al. The sickness impact profile: development of an outcome measure of health care. Am J Public Health. 1975;65:1304–10.
CAS
CrossRef
PubMed
PubMed Central
Google Scholar
Ware JE, Sherbourne CD. The MOS 36-item short-form health survey (SF-36) I. Conceptual framework and item selection. Med Care. 1992;30:473–83.
CrossRef
PubMed
Google Scholar
Brazier JE, Usherwood T, Harper R, Thomas K. Deriving a preference-based single index from the UK SF-36 health survey. J Clin Epidemiol. 1998;51:1115–28.
CAS
CrossRef
PubMed
Google Scholar
Brazier JE, Roberts J, Deverill M. The estimation of a preference-based measure of health from the SF-36. J Health Econ. 2002;21:271–92.
CrossRef
PubMed
Google Scholar
Cella DF, Tulsky DS, Gray G, et al. The functional assessment of cancer therapy scale: development and validation of the general measure. J Clin Oncol. 1993;11:570–9.
CAS
PubMed
Google Scholar
Temel JS, Greer JA, Muzikansky A, et al. Early palliative care for patients with metastatic non-small-cell lung cancer. N Engl J Med. 2010;363:733–42.
CAS
CrossRef
PubMed
Google Scholar
Brady MJ, Cella DF, Mo F, et al. Reliability and validity of the functional assessment of cancer therapy-breast quality-of-life instrument. J Clin Oncol. 1997;15:974–86.
CAS
PubMed
Google Scholar
Basen-Engquist K, Bodurka-Bevers D, Fitzgerald MA, et al. Reliability and validity of the functional assessment of cancer therapy-ovarian. J Clin Oncol. 2001;19:1809–17.
CAS
PubMed
Google Scholar
Fayers P, Bottomley A, on behalf of the EORTC Quality of Life Group and of the Quality of Life Unit. Quality of life research within the EORTC: the EORTC QLQ-C30. Eur J Cancer. 2002;38:S125–33.
Google Scholar
Vivat B, Young T, Efficace F, et al. on behalf of the EORTC Quality of Life Group. Cross-Cultural Development of the EORTC QLQ-SWB36: a stand-alone measure of spiritual well-being for palliative care in patients with cancer. Palliat Med. 2013;27:457–69.
Google Scholar
Gershon RC, Rothrock N, Hanrahan R, Bass M, Cella D. The use of PROMIS and assessment center to deliver patient-reported outcome measures in clinical research. J Appl Meas. 2010;11:304–14.
PubMed
PubMed Central
Google Scholar
Cella D, Yount S, Rothrock N, et al. The patient-reported outcomes measurement information system (PROMIS): progress of an NIH roadmap cooperative group during its first two years. Med Care. 2007;45(S1):S3–11.
CrossRef
PubMed
PubMed Central
Google Scholar
Cella D, Riley W, Stone A, et al. The patient-reported outcomes measurement information system (PROMIS) developed and tested its first wave of adult self-reported health outcome item banks: 2005–2008. J Clin Epidemiol. 2010;63:117–94.
CrossRef
Google Scholar
National Cancer Institute. Common Terminology Criteria for Adverse Events (CTCAE) Version 4.0. NIH Publication No. 09–5410. U.S. Department of Health and Human Services, National Institutes of Health, National Cancer Institute: Bethesda; 2010.
Google Scholar
Reeve BB, Mitchell SA, Dueck AC, et al. Recommended patient-reported core set of symptoms to measure in adult cancer treatment trials. J Natl Cancer Inst. 2004;106:1–8.
Google Scholar