Abstract
Gene therapy is an attractive approach for the treatment of a number of inherited and acquired disorders of the nervous system. For instance, genetic manipulations could be used to provide locally the neurotransmitters that are defective in conditions such as Parkinson’s disease, or to produce healing levels of growth factors to protect neurons against the irreversible consequences of traumatic or degenerative lesions.
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Trono, D., Blömer, U., Naldini, L. (1998). Lentiviral Vectors for Gene Delivery in the Nervous System. In: Chiocca, E.A., Breakefield, X.O. (eds) Gene Therapy for Neurological Disorders and Brain Tumors. Contemporary Neuroscience. Humana Press, Totowa, NJ. https://doi.org/10.1007/978-1-59259-478-8_7
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