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Journal of Inherited Metabolic Disease

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References

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Authors and Affiliations

  1. Department of Paediatrics and Metabolic Center, University Hospitals Leuven, Leuven, Belgium

    Peter Witters

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  1. Peter Witters
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Correspondence to Peter Witters.

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Review on Lentiviral haematopoietic stem cell gene therapy in early-onset metachromatic leukodystrophy: a new therapeutic era

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Witters, P. News and views. J Inherit Metab Dis 39, 763–764 (2016). https://doi.org/10.1007/s10545-016-9983-4

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  • DOI: https://doi.org/10.1007/s10545-016-9983-4

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